Our Association HPN France - Medullary Aplasia, created in 2004, raises funds to support research on Paroxysmal Nocturnal Hemoglobinuria (PNH) and Idiopathic Medullary Aplasia (IMA) which are two serious rare blood diseases that are "cousins" and often concomitant. We finance research grants and training for young doctors interested in these subjects. We approached the Rare Diseases Foundation (RMF) to help us find laureates with projects that would advance knowledge in these specialized and very specific areas. We worked closely with Ms. Lyne Valentino to develop a Call for Projects, to disseminate it, and to have a panel of specialists evaluate the responses that were received. Finally, we were able to award a grant of 10,000 euros to a doctor whose project, concerning an optimization of the treatment of HPN, was retained by our Association after its validation by the FMR. Then, the FMR followed for us the progress of our laureate's project and kept us informed of its progress.
We greatly appreciated the quality and responsiveness of our interactions with FMR throughout this process, and we thank them very much.